Search results

• 2018

  Short-hairpin rna against aberrant HBB^{IVSI-110(G>A)} mRNA restores β-globin levels in a novel cell model and acts as mono-and combination therapy for β-thalassemia in primary hematopoietic stem cells

  Patsali, P., Papasavva, P., Stephanou, C., Christou, S., Sitarou, M., Antoniou, M. N., Lederer, C. W. & Kleanthous, M., 31 Aug 2018, In: Haematologica. 103, 9, p. e419-e423

  Research output: Contribution to journal › Letter › peer-review
  13 Citations (Scopus)