Lentiviral-transduced HSC lead to long-term correction of beta-thalassemia by in vivo selection or erythroid progenitors.

A Miccio, R Cesari, C Rossi, F Tiboni, F Sanvito, M Ponzoni, S Routledge, M Antoniou, G Ferrari

Research output: Contribution to journalPoster abstract

Original languageEnglish
Article number250
Pages (from-to)S96 - S96
JournalMolecular Therapy
Volume15
Publication statusPublished - 2007
EventAmerican Society of Gene Therapy (ASGT) 10th Annual Meeting - Seattle, WA, United States
Duration: 30 May 20073 Jun 2007

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