Repeated AAV-mediated gene transfer by serotype switching enables long-lasting therapeutic levels of hUgt1a1 enzyme in a mouse model of Crigler-Najjar Syndrome Type i

L. Bočkor, G. Bortolussi, A. Iaconcig, G. Chiaruttini, C. Tiribelli, M. Giacca, F. Benvenuti, L. Zentilin, A. F. Muro*

*Corresponding author for this work

Research output: Contribution to journal › Article › peer-review

29 Citations (Scopus)

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Biochemistry, Genetics and Molecular Biology